There are many molecular targets available for treating TSC, but the mTOR inhibitors have just been recently added to the treatment of the disease. New<unk>  are being currently developed and investigated.
Tuberous sclerosis future or investigational therapies
Tuberous sclerosis medical therapy
Neurofibromatosis type 1 secondary prevention
Lesch-Nyhan syndrome medical therapy
Andersen-Tawil syndrome primary prevention
Progeria secondary prevention
Asperger syndrome medical therapy
Duchenne muscular dystrophy interventions