Hos seks patienter med Gauchers sygdom, type 3 var koncentrationen af miglustat i cerebrospinalvæske ved steady state 31, 4- 67, 2% af indholdet i plasma.
At steady state, the concentration of miglustat in cerebrospinal fluid of six type 3 Gaucher disease patients was 31.4– 67.2% of that in plasma.