Cystadane anvendes til patienter med alle tre former for homocystinuri, der skyldes mangel på de stoffer, der nedbryder methionin ("cystathionin- beta- syntase" eller "5, 10- methylentetrahydrofolatreduktase") eller defekter i kobalamin- kofaktorstofskiftet.
Cystadane is used in patients with all three known types of homocystinuria, caused by a lack of the substances required for the breakdown of methionine (‘ cystathionine beta-synthase’ [CBS] or ‘ 5,10- methylene-tetrahydrofolate reductase’ [MTHFR]), or by defects in ‘ cobalamin cofactor metabolism’ (cbl).