busulfan,otq923
otsuka,novartis,crispr
['otq923', 'busulfan', 'crispr']
initial #outcome otq923, an autologous, ex vivo, crispr/cas9-edited, cd34+ hematopoietic stem and progenitor cell product, #sicklecell #ash22 #nola 
Haematologist, red cell disorders and marrow failure. Working towards definitive cure: #BMT #genetherapy. @ImperialNHS @ImperialImmuno @TheEBMT @ApothecariesLDN