mitapivat
agios pharmaceuticals
['mitapivat']
13. 506 kuo &amp; : pros in pkd on mitapivat. clinically meaningful improvement in pkd-specific pros over 2 years. great example of how pros can be incorporated (and how should be reported with mcid/mids depicted!) into trials. #ash22 
#lymsm & #mmsm hematologist & patient-reported outcomes researcher @CUHematology. Founder of https://t.co/kN6qeGXfg5, @inTrainingDoc & @inHouseMag. ??????