NTLA-2001
intellia Therapeutics,regeneron
['cardio', 'cardiomyopathy', 'regeneron', 'crispr']
exciting ph1 data from for in vivo crispr gene editing of ttr in patients with attr amyloid cardiomyopathy: &gt;90% lowering of ttr serum reduction over 4-6mo #aha22 
Dir of Prev Cardiology @MassGeneralNews | Assoc Prof @harvardmed | Assoc Mem @broadinstitute | Assoc Ed @JAMACardio @ScienceAdvances