pegcetacoplan
sobi,Apellis Pharmaceuticals
['prince']
reassuring that #qol scores improved in phase 3 prince trial however there is other rich #qol information to be gathered in all #pnhdisease trials relevant to both #patients and #hta by also using disease specific #qol #eha2022 #patientsinvolved 
Paroxysmal nocturnal haemoglobinuria (PNH) patients & families in England, Wales and NI supporting one other. PNH Support is a registered CIO (no. 1161518).