NTLA-2001
Intellia Therapeutics
['cardio', 'cardiomyopathy', 'crispr']
first in-human in-vivo crispr/cas9 editing of the ttr gene by ntla-2001 in patients with attr cardiomyopathy #genetherapy #heartfailure *mainresult: &gt;90% ttr lowering* but will this translate to clinical outcomes? #aha2022 
Consultant Cardiologist in Heart Failure and Devices. Honorary Senior Clinical Lecturer ARU. #FreedomFromFailure #TheFword #BEATHF