exa-cel
Vertex pharmaceuticals,CRISPR therapeutics AG
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amazing efficacy results of #crispr gene #editing for #tbt and #scd presented at the #eha2022 congress! would also be relevant for the field to know more about graft #clonality, off-targets and long-range deletions in patients... unfortunately no reports yet 
Postdoctoral researcher at the @NaldiniLab // San Raffaele Telethon Institute for Gene Therapy, Milan ???? Views are my own.