busulfan
otsuka
['busulfan']
7/another patient with #tdt had saes of delayed neutrophil engraftment and thrombocytopenia, both of which were considered related to exa-cel and busulfan &amp; both saes have resolved. among the 31 patients with #sicklecell, there were no saes considered related to exa-cel! #ash22 
#Science & #Innovation. Special interest in #CRISPR, #GeneEditing, #GeneTherapy ?? & #Ophthalmology. #Biotech, #Markets & #Stocks ??