ctx001
vertex,crispr
['pedal', 'ctx001', '$crsp', 'vertex', '$vrtx', 'crispr']
1/ &amp; $vrtx presented an updated clinical data of exa-cel (ctx001) from 75 #patients: 44 tdt+31 #sicklecelldisease &amp; with a long follow-up. the data demonstrates that exa-cel has the potential to be a one-time functional #cure. $crsp #ash22 #geneediting #crispr #biotech 
#Science & #Innovation. Special interest in #CRISPR, #GeneEditing, #GeneTherapy ?? & #Ophthalmology. #Biotech, #Markets & #Stocks ??