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wolfgang miesbach showed the updated 2 year data on the phase 3 hope-b trial at #ash22. this is the gene therapy for #hemophilia b that was recently approved by the fda. the fix levels are remaining stable and the mean is at 2 years is 36.7%, having been 29.0% at 6 months. 
Professor of Haemostasis and Thrombosis in Sheffield, UK. I tweet about thrombosis, hemophilia, COVID-19, medicine & NHS. Opinions are my own.