Not Tagged
crispr
['crispr']
2/gph101 (nula-cel) is a #crispr #cas9 #geneediting autologous #stem #cell-based #therapy in clinical development aimed to treat #sicklecelldisease. gph101 is designed to directly correct the underlying mutation, thereby decreasing hbs production &amp; restoring hba expression #ash22 
#Science & #Innovation. Special interest in #CRISPR, #GeneEditing, #GeneTherapy ?? & #Ophthalmology. #Biotech, #Markets & #Stocks ??