exa-cel
Vertex pharmaceuticals,CRISPR therapeutics AG
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do we have a cure for #sicklecell &amp; #thalassemia? results on 75 patients with up to 3 years follow up presented at #eha2022 #eha22 and our research team for enrolling and caring for patients on this trial #genetherapy 
Deputy Physician-in-Chief of Blood Cancers @SarahCannonDocs | Director @TriStarHealth BMT Program | President @ASTCT 2019 | #BMTsm #CARTcell #CellTherapy